2025
Hoyer-Kuhn H. Oral Infigratinib in Children with Achondroplasia - Targeted Treatment. N Engl J Med. 2025 Feb 27
Spanou CES, Yang C, Godwin ARF, Morosky S, Anbalagan A, Lütke S, Mörgelin M, Marcous F, Aziz U, Wohl AP, Jabeen I, Koch M, Jowitt TA, Roman BL, Tarakanova A, Baldock C, Sengle G. Prodomain processing controls BMP-10 bioactivity and targeting to fibrillin-1 in latent conformation. FASEB J. 2025 Feb 15